Misplaced Pages

This article has multiple issues. Please help improve it or discuss these issues on the talk page. (Learn how and when to remove these messages) The topic of this article may not meet Misplaced Pages's notability guidelines for companies and organizations. Please help to demonstrate the notability of the topic by citing reliable secondary sources that are independent of the topic and provide significant coverage of it beyond a mere trivial mention. If notability cannot be shown, the article is likely to be merged, redirected, or deleted. Find sources: "TREAT-NMD" – news · newspapers · books · scholar · JSTOR (June 2018) (Learn how and when to remove this message) This article may rely excessively on sources too closely associated with the subject, potentially preventing the article from being verifiable and neutral. Please help improve it by replacing them with more appropriate citations to reliable, independent, third-party sources. (June 2018) (Learn how and when to remove this message) (Learn how and when to remove this message)

TREAT-NMD (treat NeuroMuscular Disease) is a global academic network that focuses on advancing research in neuromuscular disorders. It was established in 2007 with its coordination centre at the Newcastle University. As of 2018, the network comprises over a hundred research centres and patient organisations from 54 countries as well as independent academics and patient representatives. The network's aim is to provide infrastructure to accelerating research through supporting collaboration between its members. Its main goals include improving trial-readiness worldwide, advancing patient diagnosis and care and accelerating pre-clinical research.

Through patient registries, TREAT-NMD provides genotype–phenotype correlation between genetic mutations and neuromuscular disease burden.

References

1. Leary, Rebecca; Oyewole, Anne; Bushby, Katharine; Aartsma-Rus, Annemieke (6 July 2017). "Translational Research in Europe for the Assessment and Treatment for Neuromuscular Disorders (TREAT-NMD)". Neuropediatrics. 48 (4): 211–220. doi:10.1055/s-0037-1604110. PMID 28683502. S2CID 19283049.
2. Bushby, Katharine; Lynn, Stephen; Straub, Volker (July 2009). "Collaborating to bring new therapies to the patient--the TREAT-NMD model". Acta Myologica. 28 (1): 12–5. PMC 2859629. PMID 19772190.
3. "TREAT-NMD Alliance Members – Organizations". TREAT Neuromuscular Network. Retrieved 13 June 2018.
4. "TREAT-NMD Alliance Members – Individuals". TREAT Neuromuscular Network. Retrieved 13 June 2018.
5. "TREAT-NMD : About the TREAT-NMD network". TREAT Neuromuscular Network.
6. Willmann, Raffaella; Rüegg, Markus A.; Fairclough, Rebecca J.; Davies, Kay E; Possekel, Stefanie; Meier, Thomas (October 2008). "T.P.3.03 TREAT-NMD-Activity 7: Accelerate preclinical phase of new therapeutic treatment development". Neuromuscular Disorders (Conference abstract). 18 (9–10): 794. doi:10.1016/j.nmd.2008.06.242. S2CID 54330245.
7. Mercuri, Eugenio Maria; Mayhew, Anna G; Muntoni, Francesco; Straub, Volker; Van Ommen, Gert-Jan; Voit, Thomas; Bertini, Enrico; Bushby, Katherine (November 2008). "Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France". Neuromuscular Disorders (Workshop report). 18 (11): 894–903. doi:10.1016/j.nmd.2008.07.003. PMID 18818076.
8. Thompson R, Robertson A, Lochmüller H (2017). "Natural History, Trial Readiness and Gene Discovery: Advances in Patient Registries for Neuromuscular Disease". Rare Diseases Epidemiology: Update and Overview. Advances in Experimental Medicine and Biology. Vol. 1031. pp. 97–124. doi:10.1007/978-3-319-67144-4_5. ISBN 978-3-319-67142-0. PMID 29214567.

Further reading

• Heslop, Emma; Csimma, Cristina; Straub, Volker; McCall, John; Nagaraju, Kanneboyina; Wagner, Kathryn R.; Caizergues, Didier; Korinthenberg, Rudolf; Flanigan, Kevin M. (23 April 2015). "The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development". Orphanet Journal of Rare Diseases. 10 (1): 49. doi:10.1186/s13023-015-0258-1. PMC 4417237. PMID 25902795.
• Bladen, Catherine L.; Rafferty, Karen; Straub, Volker; Monges, Soledad; Moresco, Angélica; Dawkins, Hugh; Roy, Anna; Chamova, Teodora; Guergueltcheva, Velina (26 August 2013). "The TREAT-NMD Duchenne Muscular Dystrophy Registries: Conception, Design, and Utilization by Industry and Academia". Human Mutation. 34 (11): 1449–1457. doi:10.1002/humu.22390. PMID 23913485. S2CID 38772058.
• Aartsma-Rus, Annemieke; Mercuri, Eugenio; Vroom, Elizabeth; Balabanov, Pavel (April 2018). "Meeting report of the "Regulatory Exchange Matters" session at the 5th International TREAT-NMD Conference:: Lessons in communication: How an early dialogue between patients, regulators and academics can further therapy development for neuromuscular disorders Freiburg, Germany, 27-29 November 2017". Neuromuscular Disorders. 28 (7): 619–623. doi:10.1016/j.nmd.2018.04.009. PMID 29778308.

• Medical research organizations